TheraRadar
Data updated: May 26, 2026

DAYBUE (trofinetide)

Cytochrome P450 3A4 Inhibitors
First-in-Class Orphan Drug Priority Review Fast Track
CNS Approved 2023-03-10

Daybue is a medication used for individuals diagnosed with Rett syndrome. It is prescribed for a broad patient population, including adults and children as young as two years old. This therapy helps patients manage the symptoms associated with the condition.

Source: FDA Label • ACADIA PHARMS INC

How DAYBUE Works

The specific way trofinetide works to produce its therapeutic effects in the body is currently not fully understood. While it helps patients with Rett syndrome, the exact biological targets or pathways it influences remain unknown.

3
Indications
--
Phase 3 Trials
2
Priority Reviews
3
Years on Market

Details

Status
Prescription
First Approved
2023-03-10
Patent Cliff
2043

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Routes
ORAL
Dosage Forms
SOLUTION

Companies

Active Ingredient: TROFINETIDE

DAYBUE Approval History

2024
2025
2026
Original
New Indication
New Form
Label Update
6 FDA actions from 2023 to 2026 · 1 indication expansions
Mar 2026 SUPPL Priority
Efficacy
Aug 2025 SUPPL
Label · Labeling
Sep 2024 SUPPL
Label · Labeling

What DAYBUE Treats

1 indications

DAYBUE is approved for 1 conditions since its original approval in 2023. These indications span multiple therapeutic areas including oncology, immunology, and more.

  • Rett Syndrome
Source: FDA Label

Drugs Similar to DAYBUE

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DAYBUE STIX
TROFINETIDE
1 shared
ACADIA PHARMS INC
Shared indications:
Rett Syndrome
📋

Clinical Trial Registry

4 trials
Trial Sponsor ID Phase Status Title
NCT04776746 results posted ACP-2566-005 Ph 3 terminated Open-Label Extension Study of Trofinetide for Rett Syndrome
NCT04988867 DAFFODIL™ results posted ACP-2566-009 Ph 2, Ph 3 terminated An Open-Label Study of Trofinetide for the Treatment of Girls Two to Five Years of Age Who Have Rett Syndrome
NCT04279314 LILAC™ results posted ACP-2566-004 Ph 3 completed Open-Label Extension Study of Trofinetide for the Treatment of Girls and Women With Rett Syndrome
NCT04181723 results posted ACP-2566-003 Ph 3 completed Study of Trofinetide for the Treatment of Girls and Women With Rett Syndrome (LAVENDER™)
🔬

Active Pipeline

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Key Completed Trials

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Completed studies with published results, ranked by significance

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Trial Timeline

Full development history with FDA approval milestones

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Understanding FDA Approval Types
Count Type What it means
- ORIG Original approval - drug first enters market
- SUPPL - Efficacy New indication (new disease/condition approved)
- SUPPL - Labeling Label text changes (warnings, dosing updates)
- SUPPL - Manufacturing Production changes (new facility)
- SUPPL - Chemistry Formulation changes (new dosage strength)

Green lines in the timeline show ORIG and Efficacy approvals - the clinically meaningful milestones.

DAYBUE FDA Label Details

Indications & Usage

FDA Label (PDF)

DAYBUE is indicated for the treatment of Rett Syndrome.

View full patent landscape →
4 OB patents · 3 families · 77 international docs across 27 countries

DAYBUE Patents & Exclusivity

Latest Patent: Jan 2043
Exclusivity: Sep 2030

Patents (8 active)

US11827600*PED Expires Jan 12, 2043
US12492167*PED Expires Jan 12, 2043
US12492167 Expires Jul 12, 2042
US11827600 Expires Jul 12, 2042
US11370755*PED Expires Feb 3, 2041
US11370755 Expires Aug 3, 2040
US9212204*PED Expires Jul 27, 2032
US9212204 Expires Jan 27, 2032

Exclusivity

NCE Until Mar 2028
ODE-425 Until Mar 2030
PED Until Sep 2030
PED Until Sep 2028
Source: FDA Orange Book

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Revenue Insights

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Patent Timeline

  • Cliff: 2043
  • 8 active patents

Trial Analysis

  • Clinical trial tracking
  • Development stage analysis

Competitive Landscape

  • 1 similar drugs
  • Same target/indication analysis
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Data Sources

Data sourced from official FDA and NIH databases. Click links to verify on original sources.